Blizzard has raised over $2 million for the charity CureDuchenne, using the seemingly irresistible lure of microtransactions ...

Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

Cumberland Pharmaceuticals Inc. (NASDAQ:CPIX) released topline results from its Phase 2 FIGHT DMD trial. The study evaluated ...

Cumberland Pharmaceuticals’ Duchenne muscular dystrophy (DMD) drug has improved the amount of blood pumped by the heart, ...

Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.

Back in ye olden tymes of the 1800s, a French physician named Guillaume Duchenne de Boulogne was shocking people's faces with ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

There is an unmet need for therapies targeting Duchenne muscular dystrophy (DMD)–related heart disease, and phase 2 results ...

Sarepta's EMBARK study confirms Elevidys offers sustained Duchenne treatment benefits, including motor function improvement ...

In year two of the trial, Elevidys demonstrated statistically significant and clinically improvements across three key ...

Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...