The symptoms and effects of all of the variants of Niemann-Pick disease result from the buildup of sphingomyelin, a type of fat, in the body. Unfortunately, there is no definitive cure for Niemann ...

Xenpozyme (olipudase alfa) the first and only approved therapy for ASMD, a group of genetic disorders also known as Niemann-Pick disease, in which a fatty substance called sphingomyelin builds up ...

However, the biochemical composition of this membrane differs notably from that of the viral envelope, which is heavily ...