LIG4 syndrome is an exceptionally rare disorder caused by a genetic mutation that prevents the body from repairing damaged ...

Congenital generalized lipodystrophy (CGL) is a rare autosomal recessive disorder characterized by a near-total absence of ...

Belite Bio is a biotech firm specializing in innovative therapies for retinal degenerative eye diseases with high unmet needs ...

Pooja, a 30-year-old woman, had been battling kidney failure due to diabetes since 2022. Initially misdiagnosed with an 'O' ...

Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as haemoglobin S. Sickle cell disease changes the shape of blood cells into a crescent ...

JPMorgan Chase & Co. boosted its holdings in shares of Belite Bio, Inc (NASDAQ:BLTE – Free Report) by 7,122.7% in the 3rd ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Research analysts at Cantor Fitzgerald issued their FY2025 EPS estimates for Belite Bio in a research note issued to investors on Tuesday, January 21st. Cantor Fitzgerald analyst J. Kim forecasts that ...

San Francisco, California Friday, January 24, 2025, 11:00 Hrs [IST] ...

Jaguar Health’s Napo Pharmaceuticals and Napo Therapeutics announced that the first patient has been dosed in the independent investigator-initiated POC trial of crofelemer, Jag ...

ABSTRACT: Polycystic kidney disease (PKD) is an autosomal dominant genetic disorder that causes the formation of multiple cysts in the kidneys, leading to kidney failure. PKD is a common condition ...