The Metachromatic Leukodystrophy Initiative (MLDi) critically responds to the findings of Zhang et al. on lentivirus-modified ...

Download this infographic to learn about the key steps in lentiviral gene delivery, including tips to help scientists overcome common workflow challenges. Experts from the Women’s Brain Foundation and ...

Cell cycle re-entry of senescent breast cancer cells after CDK4/6 inhibition (CDK4/6i) constitutes a major source of disease ...

CRISPR technology has radically transformed genetic research, and at the forefront of this transformation is CRISPR screening ...

Telethon Foundation is seeking approval for a gene therapy to treat the rare disease Wiskott-Aldrich syndrome.

Oxford, UK – 5 February 2025: OXB (LSE: OXB), a quality and innovation-led cell and gene therapy CDMO, today announces the appointment of Jefferies International Limited ("Jefferies") as its Joint ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: Transfusion-dependent β-thalassemia (TDT) is a condition that results in iron ...

In a recent transaction, Richard A. Colvin, the Chief Medical (TASE:PMCN) Officer of bluebird bio, Inc. (NASDAQ:BLUE), sold shares of the company's common stock. On February 3, 2025, Colvin sold 64 ...

Thirty patients have received the gene therapy within a clinical trial and early-access program, and the foundation also hopes to seek approval in the US.

Optimized lentiviral transduction enhances gene delivery in human iPSC-derived lung organoids, enabling advanced mechanistic studies in development and disease through improved protocols validated ...

Thomas J. Klima, the Chief Commercial and Operating Officer of bluebird bio, Inc. (NASDAQ:BLUE), recently sold shares of the company’s common stock. According to a recent SEC filing, Klima disposed of ...