Evan McMenamin said his brother Travis, "never lets it get him down" despite the "incredible challenges" he faces ...

Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

Cumberland Pharmaceuticals Inc. (NASDAQ:CPIX) released topline results from its Phase 2 FIGHT DMD trial. The study evaluated ...

Some of the market’s biggest winners start off as the smallest players. While trillion-dollar tech giants like the ...

Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.

Cumberland Pharmaceuticals’ Duchenne muscular dystrophy (DMD) drug has improved the amount of blood pumped by the heart, ...

Not all growth stocks worth buying these days focus on the artificial intelligence field. There are many exciting ones in ...

There is an unmet need for therapies targeting Duchenne muscular dystrophy (DMD)–related heart disease, and phase 2 results ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Sarepta's EMBARK study confirms Elevidys offers sustained Duchenne treatment benefits, including motor function improvement ...

In year two of the trial, Elevidys demonstrated statistically significant and clinically improvements across three key ...

Blizzard has raised over $2 million for the charity CureDuchenne, using the seemingly irresistible lure of microtransactions ...